Blood-brain barrier – directed gene therapy as a strategy to treat Niemann-Pick C2 disease

Charlotte Laurfelt Munch Rasmussen, Winfried Neuhaus (Supervisor)

Research output: ThesisDoctoral Thesis

Original languageEnglish
QualificationDoctor / PhD
Awarding Institution
  • Aalborg University
Supervisors/Advisors
  • Bohn Thomsen, Louiza , Supervisor, External person
  • Neuhaus, Winfried, Supervisor
  • Olsen Alstrup, Aage Kristian , Supervisor, External person
  • Fink, Trine, Supervisor, External person
Award date3 Mar 2023
Publication statusPublished - 3 Mar 2023

Research Field

  • Molecular Diagnostics

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